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Mark Kay

13PUBLICATIONS
50CO-AUTHORS
Medical molecular engineering of nucleic acids and proteinsTransgenesisGene and molecular therapyReaction engineering (excl. nuclear reactions)Artificial life and complex adaptive systems
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Journal

Publications (13)

Sort by Publication Date:
|Mar 30, 2026
First-in-human nuclease-free homologous recombination-dependent gene editing in pediatric patients with methylmalonic acidemia: results of a phase 1/2 study.

Jirair K Bedoyan, Thomas Morgan, Angela Sun

|Dec 11, 2025
Species-specific AAVR dominates species-tropism of adeno-associated virus (AAV) vectors.

Mark Kay, Yuqian Jiang, Yiming Liu

|Nov 24, 2025
Integrated AAV optimization enables efficient gene delivery to kidney in murine and human tissue.

Fernando Gomez Garcia, Miriam Rivera Moreno, Shashank Chetty

|Oct 03, 2025
Stereo-random oligonucleotides enable efficient recruitment of ADAR in vitro and in vivo.

Laura S Pfeiffer, Tobias Merkle, Paul Vogel

|Jan 27, 2025
Operationalising a Haemophilia Gene Editing Lexicon for Practical Use.

William McKeown, Cedric Hermans, Carmen Unzu

|May 20, 2024
AAV-mediated genome editing is influenced by the formation of R-loops.

Francesco Puzzo, Magdalena P Crossley, Aranyak Goswami

Pageof 3

Frequent Collaborators

3 joint publications

Katja Pekrun

2 joint publications

Shinnosuke Tsuji

1 joint publications

Yichi Su

1 joint publications

Namdoo Kim

1 joint publications

Kerriann M Casey

1 joint publications

Thomas A Kirkland

1 joint publications

Michael Z Lin

1 joint publications

Qing-Jun Luo

1 joint publications

Pan Li

1 joint publications

Qiangfeng Cliff Zhang

Frequent Collaborators

3 joint publications

Katja Pekrun

2 joint publications

Shinnosuke Tsuji

1 joint publications

Yichi Su

1 joint publications

Namdoo Kim

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