Juan Bueren
7PUBLICATIONS
26CO-AUTHORS
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Publications (7)
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|May 28, 2025
In vivo haemopoietic stem cell gene therapy enabled by postnatal trafficking.Michela Milani, Anna Fabiano, Marta Perez-Rodriguez
|Sep 11, 2023
Advances and Challenges in the Development of Gene Therapy Medicinal Products for Rare Diseases.Juan A Bueren, Alberto Auricchio
|Feb 13, 2023
Access to gene therapy for rare diseases when commercialization is not fit for purpose.Thomas Fox, Juan Bueren, Fabio Candotti
|Nov 13, 2022
Adenine base editing efficiently restores the function of Fanconi anemia hematopoietic stem and progenitor cells.Sebastian M Siegner, Laura Ugalde, Alexandra Clemens
|Sep 11, 2019
Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia.Paula Río, Susana Navarro, Wei Wang
|Sep 14, 2017
Therapeutic gene editing in CD34+ hematopoietic progenitors from Fanconi anemia patients.Begoña Diez, Pietro Genovese, Francisco J Roman-Rodriguez
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Frequent Collaborators
4 joint publications
Paula Río
2 joint publications
Alessandro Aiuti
2 joint publications
Luigi Naldini
2 joint publications
Julián Sevilla
1 joint publications
Susana Navarro
1 joint publications
Guillermo Guenechea
1 joint publications
Alain Fischer
1 joint publications
Rosa Yañez
1 joint publications
Jose A Casado
1 joint publications
Jordi Surrallés
