Stefanie Müthel

1PUBLICATIONS
6CO-AUTHORS
Gene and molecular therapy
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Publications (1)

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|Jan 03, 2025
Gene-editing in patient and humanized-mice primary muscle stem cells rescues dysferlin expression in dysferlin-deficient muscular dystrophy.

Helena Escobar, Silvia Di Francescantonio, Julia Smirnova

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Frequent Collaborators

1 joint publications

Helena Escobar

1 joint publications

Robin Graf

1 joint publications

Andreas Marg

1 joint publications

Oliver Daumke

1 joint publications

Ralf Kühn

1 joint publications

Simone Spuler

Frequent Collaborators

1 joint publications

Helena Escobar

1 joint publications

Robin Graf

1 joint publications

Andreas Marg

1 joint publications

Oliver Daumke

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