Sylvia Fong

6PUBLICATIONS
31CO-AUTHORS
BiomaterialsGene and molecular therapyMedical devicesGenetically modified animals
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Publications (6)

|May 01, 2026
BMN 349, a small molecule inhibitor of Z alpha-1 antitrypsin polymerization, increases secretion and reduces intrahepatic inclusions in a mouse model of disease.

|Feb 02, 2026
Translational insights from nonclinical studies of AAV gene therapies for hemophilia: mechanisms underpinning variability and durability of gene expression.

Sylvia Fong, Laura L Swystun, Paul Batty

|Oct 08, 2024
Gene therapy for hemophilia.

Peter J Lenting, Sylvia Fong

|Jun 06, 2024
Optimizing liver health before and after gene therapy for hemophilia A.

Margaret V Ragni, Henry Mead, Ype P de Jong

|Mar 07, 2024
Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer.

Paul Batty, Sylvia Fong, Matteo Franco

|Apr 12, 2022
Interindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A.

Sylvia Fong, Bridget Yates, Choong-Ryoul Sihn

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Frequent Collaborators

2 joint publications

Paul Batty

2 joint publications

Laura L Swystun

2 joint publications

David Lillicrap

1 joint publications

Chris B Russell