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Blair R Leavitt

11PUBLICATIONS
39CO-AUTHORS
NeurogeneticsGene and molecular therapyMedical molecular engineering of nucleic acids and proteinsComputational neuroscience (incl. mathematical neuroscience and theoretical neuroscience)Medical infection agents (incl. prions)
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Journal

Publications (11)

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|Apr 09, 2026
Wild-type huntingtin in neurodevelopment.

Laura Lynn Chan, Blair R Leavitt

|Jan 22, 2026
Silencing of human <i>HTT</i> by targeted CRISPR/dCas9-mediated epigenetic editing.

Yi Lin Tay, Sarah B Thomson, Silvia Hnatova

|Jan 06, 2026
Oral splicing modulator branaplam in Huntington's disease: a phase 2 randomized controlled trial.

Beth Borowsky, Harry Ramos, Angelika Caputo

|Jul 02, 2025
Cell-specific mechanisms drive connectivity across the time course of Huntington's disease.

Carlos Estevez-Fraga, Isaac Sebenius, Justine Y Hansen

|Mar 28, 2025
Emerging roles of microglia and neuroinflammation in Huntington's disease: From pathophysiology to clinical trials.

Muna Abedrabbo, Pardis Kazemian, Colúm Connolly

|Mar 14, 2023
Progressive alterations in white matter microstructure across the timecourse of Huntington's disease.

Carlos Estevez-Fraga, Michael S Elmalem, Marina Papoutsi

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Frequent Collaborators

4 joint publications

Sarah J Tabrizi

3 joint publications

Sarah B Thomson

3 joint publications

Carlos Estevez-Fraga

3 joint publications

Geraint Rees

2 joint publications

Rachael I Scahill

2 joint publications

Douglas R Langbehn

2 joint publications

Roy van der Meel

2 joint publications

Pieter R Cullis

2 joint publications

Dominik Witzigmann

2 joint publications

Jayesh A Kulkarni

Frequent Collaborators

4 joint publications

Sarah J Tabrizi

3 joint publications

Sarah B Thomson

3 joint publications

Carlos Estevez-Fraga

3 joint publications

Geraint Rees

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