Nathalie Marie Goemans

9PUBLICATIONS
49CO-AUTHORS
Predictive and prognostic markersInfant and child healthMedical virologyMolecular medicineGene and molecular therapy
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Publications (9)

|May 26, 2026
A Validated Prognostic Score for Time to Loss of Ambulation in Patients With Duchenne Muscular Dystrophy.

|Oct 02, 2025
Longitudinal interaction between muscle impairments and gait pathology in growing children with Duchenne muscular dystrophy.

Ines Vandekerckhove, Geert Molenberghs, Marleen Van den Hauwe

|Feb 09, 2024
Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy: A Randomized Controlled Trial.

Utkarsh J Dang, Jesse M Damsker, Michela Guglieri

|Apr 18, 2023
Correction to: Two‑year efficacy and safety of risdiplam in patients with type 2 or non‑ambulant type 3 spinal muscular atrophy (SMA).

Maryam Oskoui, John W Day, Nicolas Deconinck

|Feb 03, 2023
Two-year efficacy and safety of risdiplam in patients with type 2 or non-ambulant type 3 spinal muscular atrophy (SMA).

Maryam Oskoui, John W Day, Nicolas Deconinck

|Feb 01, 2023
DMD Genotypes and Motor Function in Duchenne Muscular Dystrophy: A Multi-institution Meta-analysis With Implications for Clinical Trials.

Francesco Muntoni, James Signorovitch, Gautam Sajeev

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Frequent Collaborators

4 joint publications

Volker Straub

4 joint publications

Erik Niks

4 joint publications

Eugenio Mercuri

3 joint publications

Laurent Servais