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Sarah Engelbeen, Daniel O'Reilly, Davy Van De Vijver+7
Sarah Engelbeen, Svetlana Pasteuning-Vuhman, Joke Boertje-van der Meulen+6
Annemieke Aartsma-Rus
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Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides
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CRISPR/Cas9 Technology in Restoring Dystrophin Expression in iPSC-Derived Muscle Progenitors
Published on : Sep 14, 2019