Nicolas Wein

2PUBLICATIONS
1CO-AUTHORS
Neurology and neuromuscular diseasesReaction engineering (excl. nuclear reactions)
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Publications (2)

|Dec 23, 2022
Emerging Perspectives on Gene Therapy Delivery for Neurodegenerative and Neuromuscular Disorders.

Cintia Gomez Limia, Megan Baird, Maura Schwartz

|Jun 01, 2021
Absence of Significant Off-Target Splicing Variation with a U7snRNA Vector Targeting DMD Exon 2 Duplications.

Nicolas Wein, Diane M Dunn, Megan A Waldrop

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