Christian Werner
5PUBLICATIONS
13CO-AUTHORS
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Publications (5)
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|Feb 22, 2026
Pharmacodynamics, Efficacy, and Safety of Intraputaminal Eladocagene Exuparvovec Administered to Pediatric Patients With Aromatic L-Amino Acid Decarboxylase Deficiency Using an MR-Compatible Cannula: 48 Weeks of Follow-Up.Daniel J Curry, Phillip L Pearl, Scellig S D Stone
|Jan 22, 2025
REVEAL-CP: Selective Screening of Pediatric Patients for Aromatic L-Amino Acid Decarboxylase Deficiency with a Guthrie Card and In Silico Structural Modeling of One Index Case.Eugen-Matthias Strehle, Roberta Battini, Vasantha Gowda
|Sep 28, 2024
Predictors of cardiac disease in duchenne muscular dystrophy: a systematic review and evidence grading.Erik Landfeldt, Alberto Alemán, Sophia Abner
|Jul 17, 2023
Correction to: Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015-2022): 2022 interim analysis.Eugenio Mercuri, Andrés Nascimento Osorio, Francesco Muntoni
|Apr 28, 2023
Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015-2022): 2022 interim analysis.Eugenio Mercuri, Andrés Nascimento Osorio, Francesco Muntoni
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Frequent Collaborators
2 joint publications
Francesco Muntoni
2 joint publications
Heather Gordish-Dressman
1 joint publications
Erik Landfeldt
1 joint publications
Rongrong Zhang
1 joint publications
Ioannis Tomazos
1 joint publications
Eugen-Matthias Strehle
1 joint publications
Mariarita Bertoldi
1 joint publications
Phillip L Pearl
1 joint publications
Donald L Gilbert
1 joint publications
Muhammad Zafar
