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Klaus Goldhahn

1PUBLICATIONS

4CO-AUTHORS

Pharmacogenomics

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Publications (1)

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|Apr 11, 2026

Risdiplam Add-On Therapy Following Onasemnogene Abeparvovec in Children With Spinal Muscular Atrophy and 2 SMN2 Copies: A Multi-Center Case Series.

Corinna Stoltenburg, Klaus Goldhahn, Arpad von Moers

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Corinna Stoltenburg

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Angela M Kaindl

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Claudia Weiß

Frequent Collaborators

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Corinna Stoltenburg

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Arpad von Moers

1 joint publications

Angela M Kaindl

1 joint publications

Claudia Weiß

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