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Jennifer M Kwon

6PUBLICATIONS

16CO-AUTHORS

Rehabilitation engineeringNeurology and neuromuscular diseasesPacific Peoples youth and familyPharmaceutical delivery technologiesNeonatology

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Publications (6)

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|Jan 28, 2026

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial.

Jennifer M Kwon, Francina Munell, Laure Le Goff

|Dec 08, 2025

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial.

Jennifer M Kwon, Francina Munell, Laure Le Goff

|Nov 10, 2025

Onasemnogene abeparvovec gene therapy for treatment of patients with spinal muscular atrophy: Updated real-world practical considerations.

Crystal M Proud, Elizabeth A Kichula, Susan E Matesanz

|Jan 10, 2024

Development and assessment of educational materials for spinal muscular atrophy carrier screening in the Plain community.

Carly Eichten, Ashley Kuhl, Mei Baker

|May 14, 2022

An expanded access program of risdiplam for patients with Type 1 or 2 spinal muscular atrophy.

Jennifer M Kwon, Kapil Arya, Nancy Kuntz

|Jan 23, 2016

Newborn screening for Krabbe disease in New York State: the first eight years' experience.

Joseph J Orsini, Denise M Kay, Carlos A Saavedra-Matiz

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Frequent Collaborators

3 joint publications

Crystal M Proud

2 joint publications

Gemma Williams

2 joint publications

Ian R Woodcock

2 joint publications

Liesbeth De Waele

2 joint publications

Tamaki Kato

1 joint publications

Chad Biski

1 joint publications

Monica Martin

1 joint publications

Aravindhan Veerapandiyan

1 joint publications

Vamshi K Rao

1 joint publications

Carly Eichten

Frequent Collaborators

3 joint publications

Crystal M Proud

2 joint publications

Gemma Williams

2 joint publications

Ian R Woodcock

2 joint publications

Liesbeth De Waele

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