Heather L Gray-Edwards

7PUBLICATIONS

51CO-AUTHORS

Gene and molecular therapyGenetically modified animalsMetabolic medicineNeurogenetics

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Publications (7)

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|May 23, 2026

Long-term comparative analysis of AAV9-mediated gene replacement therapies for spinal muscular atrophy in mice.

|Sep 11, 2025

Treatment of a severe vascular disease using a bespoke CRISPR-Cas9 base editor in mice.

Christiano R R Alves, Sabyasachi Das, Vijai Krishnan

|Aug 15, 2025

Dual-vector rAAVrh8 gene therapy for GM2 gangliosidosis: a phase 1/2 trial.

Florian Eichler, Oguz I Cataltepe, Rrita Daci

|Feb 26, 2025

<i>BCKDHA-BCKDHB</i> digenic gene therapy restores metabolic homeostasis in two mouse models and a calf with classic maple syrup urine disease.

Jiaming Wang, Laura E Poskitt, Jillian Gallagher

|Sep 26, 2024

Neuroimaging Applications for the Delivery and Monitoring of Gene Therapy for Central Nervous System Diseases.

Rrita Daci, Heather Gray-Edwards, Mohammed Salman Shazeeb

|Sep 08, 2022

Redosing Adeno-Associated Virus Gene Therapy to the Central Nervous System.

Abigail McElroy, Miguel Sena-Esteves, Motahareh Arjomandnejad

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Frequent Collaborators

Jun Xie

Thomas L Gallagher

Allison M Keeler

Guangping Gao

Jiaming Wang

Laura E Poskitt

Phillip W L Tai

Karlla W Brigatti

William C Baker

Hector R Benatti

Frequent Collaborators

Jun Xie

Thomas L Gallagher

Allison M Keeler

Guangping Gao