Heather L Gray-Edwards

7PUBLICATIONS
51CO-AUTHORS
Gene and molecular therapyGenetically modified animalsMetabolic medicineNeurogenetics
Featured researcher

Get your video featured.

JoVEPublish with JoVE
Journal

Publications (7)

|Sep 11, 2025
Treatment of a severe vascular disease using a bespoke CRISPR-Cas9 base editor in mice.

Christiano R R Alves, Sabyasachi Das, Vijai Krishnan

|Aug 15, 2025
Dual-vector rAAVrh8 gene therapy for GM2 gangliosidosis: a phase 1/2 trial.

Florian Eichler, Oguz I Cataltepe, Rrita Daci

|Feb 26, 2025
BCKDHA-BCKDHB digenic gene therapy restores metabolic homeostasis in two mouse models and a calf with classic maple syrup urine disease.

Jiaming Wang, Laura E Poskitt, Jillian Gallagher

|Sep 26, 2024
Neuroimaging Applications for the Delivery and Monitoring of Gene Therapy for Central Nervous System Diseases.

Rrita Daci, Heather Gray-Edwards, Mohammed Salman Shazeeb

|Sep 08, 2022
Redosing Adeno-Associated Virus Gene Therapy to the Central Nervous System.

Abigail McElroy, Miguel Sena-Esteves, Motahareh Arjomandnejad

Pageof 2