Hasane Ratni

6PUBLICATIONS
9CO-AUTHORS
Gene and molecular therapyBiomolecular modelling and designProteins and peptidesMolecular medicine
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Publications (6)

|May 30, 2026
Tunable gene control via RNA splicing with a clinically approved small molecule.

|Jun 18, 2021
Risdiplam, the First Approved Small Molecule Splicing Modifier Drug as a Blueprint for Future Transformative Medicines.

Hasane Ratni, Renata S Scalco, Alexander H Stephan

|Jun 14, 2021
Phenyl bioisosteres in medicinal chemistry: discovery of novel γ-secretase modulators as a potential treatment for Alzheimer's disease.

H Ratni, K Baumann, P Bellotti

|Jan 18, 2020
Discovery of Balovaptan, a Vasopressin 1a Receptor Antagonist for the Treatment of Autism Spectrum Disorder.

Patrick Schnider, Caterina Bissantz, Andreas Bruns

|Jul 26, 2018
Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 ( SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA).

Hasane Ratni, Martin Ebeling, John Baird

|Apr 26, 2017
Discovery of a Novel Class of Survival Motor Neuron 2 Splicing Modifiers for the Treatment of Spinal Muscular Atrophy.

Emmanuel Pinard, Luke Green, Michael Reutlinger

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Frequent Collaborators

1 joint publications

P Bellotti

1 joint publications

X A Cook

1 joint publications

Patrick Schnider

1 joint publications

Alexander H Stephan