Hasane Ratni

6PUBLICATIONS

9CO-AUTHORS

Gene and molecular therapyBiomolecular modelling and designProteins and peptidesMolecular medicine

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Publications (6)

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|May 30, 2026

Tunable gene control via RNA splicing with a clinically approved small molecule.

|Jun 18, 2021

Risdiplam, the First Approved Small Molecule Splicing Modifier Drug as a Blueprint for Future Transformative Medicines.

Hasane Ratni, Renata S Scalco, Alexander H Stephan

|Jun 14, 2021

Phenyl bioisosteres in medicinal chemistry: discovery of novel γ-secretase modulators as a potential treatment for Alzheimer's disease.

H Ratni, K Baumann, P Bellotti

|Jan 18, 2020

Discovery of Balovaptan, a Vasopressin 1a Receptor Antagonist for the Treatment of Autism Spectrum Disorder.

Patrick Schnider, Caterina Bissantz, Andreas Bruns

|Jul 26, 2018

Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 ( SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA).

Hasane Ratni, Martin Ebeling, John Baird

|Apr 26, 2017

Discovery of a Novel Class of Survival Motor Neuron 2 Splicing Modifiers for the Treatment of Spinal Muscular Atrophy.

Emmanuel Pinard, Luke Green, Michael Reutlinger

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Frequent Collaborators

P Bellotti

X A Cook

Patrick Schnider

Alexander H Stephan

Mateusz Mendel

Dominic Schwarz

Martin Ebeling

Filip Roudnicky

Lina Schukur

Frequent Collaborators

P Bellotti

X A Cook

Patrick Schnider

Alexander H Stephan