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Kenneth H Fischbeck

3PUBLICATIONS
22CO-AUTHORS
PainGene and molecular therapy
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Publications (3)

Sort by Publication Date:
|Aug 14, 2024
Patient-Reported Impact of Symptoms in Spinal and Bulbar Muscular Atrophy.

Abdullah Alqahtani, Angela Kokkinis, Christine Zizzi

|Aug 21, 2021
Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity.

Wooi F Lim, Mitra Forouhan, Thomas C Roberts

|Feb 15, 2020
Combinatorial treatment for spinal muscular atrophy: An Editorial for 'Combined treatment with the histone deacetylase inhibitor LBH589 and a splice-switch antisense oligonucleotide enhances SMN2 splicing and SMN expression in Spinal Muscular Atrophy cells' on page 264.

Angelo Poletti, Kenneth H Fischbeck

Pageof 1

Frequent Collaborators

1 joint publications

Angelo Poletti

1 joint publications

Wooi F Lim

1 joint publications

Thomas C Roberts

1 joint publications

Jesse Dabney

1 joint publications

Alfina A Speciale

1 joint publications

Raquel Manzano

1 joint publications

Gavinda Sangha

1 joint publications

Mariana Conceição

1 joint publications

Lara Cravo

1 joint publications

Annabelle Biscans

Frequent Collaborators

1 joint publications

Angelo Poletti

1 joint publications

Wooi F Lim

1 joint publications

Thomas C Roberts

1 joint publications

Jesse Dabney

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