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Louise R Rodino-Klapac

3PUBLICATIONS

19CO-AUTHORS

Gene and molecular therapyMedical virology

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Publications (3)

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|Jun 04, 2026

Five-Year Outcomes With Delandistrogene Moxeparvovec in Patients With Duchenne Muscular Dystrophy: A Phase 1/2a Study.

|Oct 09, 2024

AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial.

Jerry R Mendell, Francesco Muntoni, Craig M McDonald

|Jan 04, 2024

Gene therapy with bidridistrogene xeboparvovec for limb-girdle muscular dystrophy type 2E/R4: phase 1/2 trial results.

Jerry R Mendell, Eric R Pozsgai, Sarah Lewis

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Frequent Collaborators

2 joint publications

Linda P Lowes

2 joint publications

Megan A Iammarino

2 joint publications

Craig M McDonald

1 joint publications

Kelly J Lehman

1 joint publications

Natalie F Reash

1 joint publications

Jerry R Mendell

1 joint publications

Francesco Muntoni

1 joint publications

Hirofumi Komaki

1 joint publications

Carmen Leon-Astudillo

1 joint publications

Crystal Proud

Frequent Collaborators

2 joint publications

Linda P Lowes

2 joint publications

Megan A Iammarino

2 joint publications

Craig M McDonald

1 joint publications

Kelly J Lehman