Theodora Markati

2PUBLICATIONS
7CO-AUTHORS
Neurology and neuromuscular diseases
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Publications (2)

|Dec 16, 2022
Early clinical and pre-clinical therapy development in Nemaline myopathy.

Gemma Fisher, Laurane Mackels, Theodora Markati

|Mar 22, 2022
Risdiplam: an investigational survival motor neuron 2 (SMN2) splicing modifier for spinal muscular atrophy (SMA).

Theodora Markati, Gemma Fisher, Sithara Ramdas

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