Marlen Lauffer

5PUBLICATIONS
5CO-AUTHORS
Gene and molecular therapyNeurology and neuromuscular diseasesMolecular medicineMedical molecular engineering of nucleic acids and proteins
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Publications (5)

|Oct 27, 2025
Individualized therapy development for rare diseases: individualized at every step of the way.

Marlen C Lauffer, Tim Yu, Annemieke Aarstma-Rus

|Apr 14, 2025
Treatability of the KMT2-Associated Neurodevelopmental Disorders Using Antisense Oligonucleotide-Based Treatments.

Bianca Zardetto, Willeke van Roon-Mom, Annemieke Aartsma-Rus

|Apr 14, 2025
Practical Recommendations for the Selection of Patients for Individualized Splice-Switching ASO-Based Treatments.

Bianca Zardetto, Marlen C Lauffer, Willeke van Roon-Mom

|Jan 05, 2024
Possibilities and limitations of antisense oligonucleotide therapies for the treatment of monogenic disorders.

Marlen C Lauffer, Willeke van Roon-Mom, Annemieke Aartsma-Rus

|Jan 20, 2023
Development of tailored splice-switching oligonucleotides for progressive brain disorders in Europe: development, regulation, and implementation considerations.

Annemieke Aartsma-Rus, Willeke van Roon-Mom, Marlen Lauffer

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Frequent Collaborators

4 joint publications

Annemieke Aartsma-Rus

3 joint publications

Willeke van Roon-Mom

2 joint publications

Bianca Zardetto

1 joint publications

Matthis Synofzik