Benjamin Liou

2PUBLICATIONS
9CO-AUTHORS
Neurology and neuromuscular diseasesGenetically modified animals
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Publications (2)

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|Jun 23, 2026
Patient-specific midbrain organoids with CRISPR correction recapitulate neuronopathic Gaucher disease phenotypes and enable evaluation of novel therapies.

|Dec 27, 2022
PGRN deficiency exacerbates, whereas a brain penetrant PGRN derivative protects, <i>GBA1</i> mutation-associated pathologies and diseases.

Xiangli Zhao, Yi Lin, Benjamin Liou

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Frequent Collaborators

2 joint publications

Yi Lin

2 joint publications

Ying Sun

1 joint publications

Xiangli Zhao

1 joint publications

Kenneth D R Setchell

1 joint publications

Gregory A Grabowski

1 joint publications

Jason Tchieu

1 joint publications

Ahmet Kaynak

1 joint publications

Xiaoyang Qi

1 joint publications

Ricardo A Feldman

Frequent Collaborators

2 joint publications

Yi Lin

2 joint publications

Ying Sun

1 joint publications

Xiangli Zhao

1 joint publications

Kenneth D R Setchell

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