Michael A Pendergast

2PUBLICATIONS
18CO-AUTHORS
Gene and molecular therapyMedical molecular engineering of nucleic acids and proteins
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Publications (2)

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|Apr 27, 2026
Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells.

|Feb 07, 2025
Base editing HbS to HbG-Makassar improves hemoglobin function supporting its use in sickle cell disease.

Zachary Kostamo, Manuel A Ortega, Chavonna Xu

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Frequent Collaborators

2 joint publications

Vivien A Sheehan

1 joint publications

Manuel A Ortega

1 joint publications

Elizabeth Budak

1 joint publications

Celeste K Kanne

1 joint publications

Ashwin Patel

1 joint publications

John Manis

1 joint publications

Giuseppe Ciaramella

1 joint publications

S Haihua Chu

1 joint publications

Kun Jia

1 joint publications

Rachel Choi

Frequent Collaborators

2 joint publications

Vivien A Sheehan

1 joint publications

Manuel A Ortega

1 joint publications

Elizabeth Budak

1 joint publications

Celeste K Kanne

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