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Flavia De Toni, Vanessa Ragaglia, Devin Schecter+9
Flavia De Toni
Vanessa Ragaglia
Xin Xu
R Mark Payne
Matthew G Baile
Gopi Shankar
Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides
Published on : May 07, 2020