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Rashmi Mathur

1PUBLICATIONS
12CO-AUTHORS
Molecular medicine
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Journal

Publications (1)

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|May 15, 2026
Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys.

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Frequent Collaborators

1 joint publications

Jean K Mah

1 joint publications

Hernan D Gonorazky

1 joint publications

Elisa Nigro

1 joint publications

Hanns Lochmüller

1 joint publications

Alberto Alemán

1 joint publications

Maryam Oskoui

1 joint publications

Anne Marie Sbrocchi

1 joint publications

Kathryn A Selby

1 joint publications

Ekaterina Gresko

1 joint publications

Aki Linden

Frequent Collaborators

1 joint publications

Jean K Mah

1 joint publications

Hernan D Gonorazky

1 joint publications

Elisa Nigro

1 joint publications

Hanns Lochmüller