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Justin Lee, Adrian Kielhorn, Sami Fam+2
Adrian Kielhorn
Eoin P Flanagan
Norio Chihara
Naoki Numajiri
Tatsuro Misu
Lumbar Intrathecal Injection of SOD1-ASOs for Precise CNS Targeting and Predictive Efficacy in Human SOD1-G93A ALS Mice
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