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BIOTECNOLOGÍA: Grupo de Enfermedades Invierte en Medicamentos para Hacerlo Usted Mismo
Science (New York, N.Y.)
|September 11, 2007
Resumen
La Fundación de Fibrosis Quística está invirtiendo 30 millones de dólares para descubrir nuevos tratamientos para la FQ. Esta iniciativa, apoyada por la Fundación Gates, pone de relieve los grupos de pacientes que impulsan la investigación biomédica.
Área de la Ciencia:
- Investigación biomédica en la investigación biomédica.
- Descubrimiento de Drogas Descubrimiento de Drogas
- Defensa de los pacientes.
Sus antecedentes:
- La fibrosis quística (FQ) es un trastorno genético que requiere nuevas estrategias terapéuticas.
- Los grupos de defensa de los pacientes están cada vez más involucrados en la financiación y dirección de la investigación.
Objetivo del estudio:
- Identificar nuevos compuestos para el tratamiento de la fibrosis quística.
- Fomentar la colaboración entre las fundaciones de pacientes y las empresas de biotecnología.
Principales métodos:
- Inversión de 30 millones de dólares por parte de la Fundación para la Fibrosis Quística en Aurora Biosciences.
- Aprovechando una donación de 20 millones de dólares de la Fundación Bill y Melinda Gates.
Principales resultados:
- Iniciación de un importante proyecto de investigación centrado en el descubrimiento de fármacos para la FQ.
- Establecimiento de una asociación entre una importante fundación de pacientes y una empresa de biotecnología.
Conclusiones:
- Los modelos de financiación liderados por el paciente pueden acelerar la investigación biomédica.
- Las inversiones estratégicas pueden impulsar el desarrollo de tratamientos para enfermedades raras como la FQ.
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