Burosumab versus terapia convencional en niños con hipofosfatemia ligada al X: ensayo aleatorizado, controlado

Erik A Imel1, Francis H Glorieux2, Michael P Whyte3

  • 1Department of Medicine and Department of Pediatrics, Indiana University School of Medicine, Indianapolis, IN, USA.

PubMed
Resumen

Burosumab mejoró significativamente la gravedad y el crecimiento del raquitismo en niños con hipofosfatemia ligada al X en comparación con la terapia convencional. Este estudio destaca el burosumab como un tratamiento más eficaz para este trastorno genético raro.

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