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Las catepsinas B y L recombinantes promueven el aclaramiento de la α-sinucleína y restauran la función lisosómica en modelos humanos y murinos con patología de la α-sinucleína
- Denise Balta 1, Anish Varghese 1, Susy Prieto Huarcaya 1, Alessandro Di Spiezio 2, André R A Marques 3, Enes Yağız Akdaş 4, Doğa Tabakacilar 5, Alice Drobny 1, Christian Werner 6, Wei Xiang 1, Rebecca Mächtel 1, Jan Philipp Dobert 1, Anna Fejtova 4, Franziska Richter 7, Melanie Küspert 5, Philipp Arnold 8, Paul Saftig 9, Friederike Zunke 10
- 1Department of Molecular Neurology, University Hospital Erlangen, Friedrich-Alexander University Erlangen-Nürnberg (FAU), Erlangen, Germany.
- 2Neuroscience Institute, National Research Council (CNR), Padua, Italy.
- 3iNOVA4Health, NOVA Medical School, NOVA University Lisbon, Lisboa, Portugal.
- 4Department of Psychiatry and Psychotherapy, University Hospital Erlangen, Friedrich-Alexander University Erlangen-Nürnberg (FAU), Erlangen, Germany.
- 5Institute of Biochemistry, Friedrich-Alexander University Erlangen- Nürnberg (FAU), Erlangen, Germany.
- 6Department of Biotechnology and Biophysics, University of Würzburg, Biocenter, Am Hubland, Würzburg, Germany.
- 7Department of Pharmacology, Toxicology and Pharmacy, University of Veterinary Medicine Hannover (TiHo), Hannover, Germany.
- 8Institute of Functional and Clinical Anatomy, Friedrich-Alexander University Erlangen-Nürnberg (FAU), Erlangen, Germany.
- 9Institute of Biochemistry, Christian-Albrechts-University Kiel, Kiel, Germany.
- 10Department of Molecular Neurology, University Hospital Erlangen, Friedrich-Alexander University Erlangen-Nürnberg (FAU), Erlangen, Germany. friederike.zunke@fau.de.
- 0Department of Molecular Neurology, University Hospital Erlangen, Friedrich-Alexander University Erlangen-Nürnberg (FAU), Erlangen, Germany.
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