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Updated: Jul 13, 2026

Primordial Germ Cell Transplantation for CRISPR/Cas9-based Leapfrogging in Xenopus
05:34

Primordial Germ Cell Transplantation for CRISPR/Cas9-based Leapfrogging in Xenopus

Published on: February 1, 2018

核移植と細胞と遺伝子療法の組み合わせによる遺伝的欠陥の修正

William M Rideout1, Konrad Hochedlinger, Michael Kyba

  • 1Whitehead Institute for Biomedical Research, 9 Cambridge Center, Cambridge, MA 02142, USA.

Cell
|April 17, 2002
PubMed
まとめ

この研究は,胚性幹細胞のRag2遺伝子を修復することによって,免疫不全に対する新しい遺伝子治療アプローチを示しています. この方法は,マウスの免疫機能を成功裏に回復させ,遺伝疾患の潜在的な治療法を提供しました.

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Lentiviral Vector-mediated Gene Therapy of Hepatocytes Ex Vivo for Autologous Transplantation in Swine09:54

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