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Updated: Feb 19, 2026

Direct Intrathecal Injection of Recombinant Adeno-associated Viruses in Adult Mice
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エダラボン:ALS の ため の 承認 さ れ た 新しい 薬

Jeffrey D Rothstein1

  • 1Brain Science Institute and Dept of Neurology, Johns Hopkins University, Baltimore, MD 21218, USA.

Cell
|November 4, 2017
PubMed
まとめ

アミオトロフィック横筋硬化症 (ALS) は致命的な神経変性疾患です. ALSに対する薬剤の発見は困難であり,FDAが承認した薬剤はリルゾールとエダラボーンだけで,疾患の進行を抑制する効果を示している.

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