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Updated: Dec 30, 2025

Implementation of Non-invasive Point of Care Transient Elastography for Evaluation of Liver Disease in Pediatric Populations with Cystic Fibrosis
05:56

Implementation of Non-invasive Point of Care Transient Elastography for Evaluation of Liver Disease in Pediatric Populations with Cystic Fibrosis

Published on: August 29, 2025

385

囊性線維症 の 大多数 の 人 の ため の 治療

Christine E Bear1

  • 1Program of Molecular Medicine and the Program for Individualized Therapy at SickKids Hospital (CFIT), The Hospital for Sick Children, Toronto, ON, Canada; Departments of Physiology and Biochemistry, University of Toronto, Toronto, ON, Canada.

Cell
|January 25, 2020
PubMed
まとめ

TRIKAFTAは,F508del変異による欠陥を修正することによって,システィック線維症 (CF) を治療するFDAが承認した新しい薬です. この変異のコピーが"つか2つある CF患者には有効です

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Managing Chronic Obstructive Pulmonary Disease (COPD) involves a multifaceted approach to reduce symptoms, prevent exacerbations, improve overall health status, and slow disease progression. Key strategies include lifestyle modifications, pharmacotherapy, supportive therapies, and, in some cases, surgery. Here is an overview of the primary COPD management strategies:
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