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Updated: Jul 14, 2026

Protein Transfection of Mouse Lung
04:21

Protein Transfection of Mouse Lung

Published on: May 15, 2013

アルファ1-アンチトリプシン欠乏症に対する毎月の増強療法の生化学的有効性および安全性

R C Hubbard1, S Sellers, D Czerski

  • 1Pulmonary Branch, National Heart, Lung, and Blood Institute, Bethesda, MD 20892.

JAMA
|September 2, 1988
PubMed
まとめ

アルファ1-アンチトリプシン (アルファ1AT) の月間注入は,アルファ1AT欠乏症のエムフィゼマを効果的に予防します. このアプローチは,保護性肺レベルを維持し,この遺伝性疾患に対する週間の治療に有効な代替案を提供します.

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