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Updated: Aug 4, 2025

Efficient PAM-Less Base Editing for Zebrafish Modeling of Human Genetic Disease with zSpRY-ABE8e
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Efficient PAM-Less Base Editing for Zebrafish Modeling of Human Genetic Disease with zSpRY-ABE8e

Published on: February 17, 2023

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免疫 の 生まれつき の 欠陥 の ため の 遺伝子 療法: 塩基 編集 が 登場 する

Harry L Malech1, Luigi D Notarangelo1

  • 1Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA.

Cell
|March 31, 2023
PubMed
まとめ

アデニン塩基編集は 精密に変異を修正し より効率的な遺伝子編集ソリューションを提供します この高度なCRISPR-Cas9技術は 標準的な方法と比較して 望ましくない遺伝的変化を減らすことができます

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