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Updated: Sep 10, 2025

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プログラム可能な自己複製型JEVナノセラピーは,ALSにおけるRNA伝達を再定義する

Yan Shan Loo1, Nur Aininie Yusoh2, Keyin Yap1

  • 1School of Science, Monash University Malaysia, Jalan Lagoon Selatan, Selangor, Malaysia.

Communications biology
|August 26, 2025
PubMed
まとめ

設計された日本脳炎ウイルス (JEV) は,アミオトロフィック横筋硬化症 (ALS) の治療のために,反感覚オリゴヌクレオチド (ASO) をモーターニューロンに届けることができる. この新しいナノキャリア戦略は 標的型で持続的な遺伝子治療を 血脳障壁を越えることを目指しています

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