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Updated: Sep 10, 2025

Subretinal Transplantation of Human Embryonic Stem Cell-Derived Retinal Tissue in a Feline Large Animal Model
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Published on: August 5, 2021

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網膜炎の遺伝子療法:現在の進歩と将来の方向性

Zofia Pniakowska1,2, Natasza Dzieża1, Natalia Kustosik1

  • 1Department of Ophthalmology and Vision Rehabilitation, Medical University of Lodz, 90-549 Lodz, Poland.

Journal of clinical medicine
|August 28, 2025
PubMed
まとめ

特定の変異を標的とした遺伝子療法や 光遺伝学のような新しいアプローチで 網膜炎の治療法が進歩しています これらの革新的な戦略は 遺伝性網膜疾患の患者の視力を保つのに 希望を与えてくれます

キーワード:
CRISPRについてルクストルナMCO-010 についてオーケストラ400QR-1123 についてSPVN06 について遺伝子療法遺伝性網膜疾患眼科についてretinitis pigmentosa レチニティス・ピグメント

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Limbal Approach-Subretinal Injection of Viral Vectors for Gene Therapy in Mice Retinal Pigment Epithelium06:48

Limbal Approach-Subretinal Injection of Viral Vectors for Gene Therapy in Mice Retinal Pigment Epithelium

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