関連する実験動画

Updated: Sep 9, 2025

Posterior Semicircular Canal Approach for Inner Ear Gene Delivery in Neonatal Mouse
03:52

Posterior Semicircular Canal Approach for Inner Ear Gene Delivery in Neonatal Mouse

Published on: March 2, 2018

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臨床的遺伝子療法による聴覚回復: パラダイムシフト

Shuang Han1, Ziting Chen1, Daqi Wang1

  • 1ENT Institute and Department of Otorhinolaryngology, Eye & ENT Hospital, Fudan University, Shanghai, China; NHC Key Laboratory of Hearing Medicine, Fudan University, Shanghai, China; Institutes of Biomedical Science, Fudan University, Shanghai, China; State Key Laboratory of Brain Function and Disorders and MOE Frontiers Center for Brain Science, Fudan University, Shanghai, China; Shanghai Key Laboratory of Gene Editing and Cell Therapy for Rare Diseases, Fudan University, Shanghai, China.

Trends in molecular medicine
|September 4, 2025
PubMed
まとめ

オートソーム性後退性失聴症9 (DFNB9) の遺伝子治療は急速な進展を示しています. OTOF変異に対する臨床試験は 遺伝性聴覚障害 (HHL) の治療法を変化させ,将来の治療法の枠組みを確立しています.

キーワード:
DFNB9 について臨床試験遺伝子療法遺伝的な聴覚障害

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