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Updated: May 3, 2026

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レンチウイルス媒介の遺伝子補充は病原性ABCA3の変種を救う

Ashley L Cooney, Shakayla Lamer, Ping Yang

    bioRxiv : the preprint server for biology
    |September 5, 2025
    PubMed
    まとめ

    重度の肺疾患の原因であるABCA3欠乏症に対して 遺伝子添加療法が有望であることが示されています ABCA3の補充により,特定のモデルでは細胞機能が部分的に回復し,炎症が軽減されました.

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