関連する実験動画

Updated: Feb 14, 2026

Ultrahigh Resolution Mouse Optical Coherence Tomography to Aid Intraocular Injection in Retinal Gene Therapy Research
10:10

Ultrahigh Resolution Mouse Optical Coherence Tomography to Aid Intraocular Injection in Retinal Gene Therapy Research

Published on: November 2, 2018

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RPE65-網膜変性症の若い患者における遺伝子療法のアウトカム

Kirk A J Stephenson1, Abrar K Alsalamah2, Anupreet Tumber1

  • 1Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada.

Canadian journal of ophthalmology. Journal canadien d'ophtalmologie
|February 12, 2026
PubMed
まとめ

Voretigene neparvovec-rzyl (VN) 遺伝子治療は,RPE65-LCAの若い患者の網膜の感受性を安全に改善します. コリオレチネス縮が起こりましたが,機能的アウトカムはポジティブであり続け,VNを証明しました.

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