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Updated: Feb 17, 2026

Interview: Glycolipid Antigen Presentation by CD1d and the Therapeutic Potential of NKT cell Activation
18:08

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Published on: December 31, 2007

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免疫の先天性欠陥に対する遺伝子治療:過去の進展,現在の状態,将来の方向性

Robert Torrance1, Kate Orf1,2, Thomas A Fox1,2

  • 1UCL Institute of Immunity and Transplantation, UCL, London NW3 2PP, United Kingdom.

Rare disease and orphan drugs journal
|February 16, 2026
PubMed
まとめ

遺伝子療法 (GT) は,遺伝的欠陥を修正して,免疫の先天性エラー (IEI) に対する,ドナーから独立した,安全で効果的な治療法を提供します. このレビューは,40年間の進歩,現在の遺伝子編集技術,IEI治療の将来の方向性を強調しています.

キーワード:
遺伝子治療は遺伝子療法です.免疫の先天的な誤りです.一次性免疫不全症によるものです.

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