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Updated: Aug 18, 2026

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1型および3型ゴーシェ病の酵素置換療法

B Bembi1, M Zanatta, M Carrozzi

  • 1Istituto di Clinica Pediatrica, Università di Trieste, IRCCS Burlo Garofolo, Italy.

Lancet (London, England)
|December 17, 1994
PubMed
まとめ

アルグルセラーゼによる酵素置換療法は,神経学的関わりのある患者を含む,ゴッシャー病の患者を改善しました. 低用量,週2回の注入は,タイプ1のゴッシャー病に有効であり,治療費を削減します.

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