骨髓移植对儿童发病的脑X链 adrenoleukodystrophy 的长期影响

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Updated: Jul 24, 2026

An In Vitro Model for the Study of Cellular Pathophysiology in Globoid Cell Leukodystrophy
07:45

An In Vitro Model for the Study of Cellular Pathophysiology in Globoid Cell Leukodystrophy

Published on: October 21, 2014

E Shapiro1, W Krivit, L Lockman

  • 1Division of Paediatric Neurology, University of Minnesota, Minneapolis 55455, USA.

Lancet (London, England)
|November 21, 2000
PubMed
概括

骨髓移植可以阻止儿童大脑X链 adrenoleukodystrophy 的渐进性脱髓化. 这种治疗提供长期益处,稳定神经功能,并在早期进行时改善结果.

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