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在患有法布里病的患者中使用阿加尔酶α的酶替代疗法:对注册数据的分析

A Mehta1, M Beck, P Elliott

  • 1University College London, London, UK. atul.mehta@royalfree.nhs.uk

Lancet (London, England)
|December 5, 2009
PubMed
概括

用阿加尔酶阿尔法进行为期五年的酶替代疗法显著有利于患有法布里病的患者,改善心脏功能,减少疼痛,提高生活质量. 与没有酶替代疗法相比,这种治疗提供了实质性的临床优势.

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