退

Rajendra S Apte1

  • 1Washington University School of Medicine, 660 South Euclid Avenue, Box 8096, St. Louis, MO 63110, USA.

Cell
|March 24, 2018
PubMed
概括

使用腺病毒载体的基因治疗将正常的RPE65蛋白传递给视网膜细胞. 这种治疗恢复了由RPE65基因突变引起的遗传视网膜退化症患者的视觉循环和视力.

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