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Updated: Jul 17, 2026

Selective Depletion of Microglia from Cerebellar Granule Cell Cultures Using L-leucine Methyl Ester
08:10

Selective Depletion of Microglia from Cerebellar Granule Cell Cultures Using L-leucine Methyl Ester

Published on: July 7, 2015

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尼曼-皮克型C的N-乙-L-氨酸:一项多国双盲随机化,安慰剂控制的交叉研究

T Fields1, T M Bremova2, I Billington3

  • 1IntraBio Ltd, Begbroke Science Park, Begroke Hill, Woodstock Road, Oxford, OX5 1PF, UK. tfields@intrabio.com.

Trials
|May 29, 2023
PubMed
概括

尼曼-皮克病C型 (NPC) 是一种罕见的神经退行性疾病. 本研究评估了N-乙-氨酸 (IB1001) 用于NPC患者的慢性症状治疗,基于之前的积极结果.

关键词:
大脑小脑动症lysosomal 储存疾病 lysosomal 储存疾病这是一种N-乙-L-氨酸.尼曼 - 皮克C型 (NPC) 公司药物干预是药物干预的方法.随机对照试验是随机对照试验.症状治疗 症状治疗

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