相关实验视频

Updated: Jul 27, 2025

Subconjunctival Administration of Adeno-associated Virus Vectors in Small Animal Models
06:16

Subconjunctival Administration of Adeno-associated Virus Vectors in Small Animal Models

Published on: March 16, 2022

3.0K

腺相关病毒 (AAV) - 基于视网膜疾病的基因疗法:我们在哪里?

Divya Ail1, Hugo Malki1, Emilia A Zin1

  • 1Sorbonne Université, INSERM, CNRS, Department of Therapeutics, Institut de la Vision, Paris, 75012, France.

The application of clinical genetics
|June 5, 2023
PubMed
概括

腺相关病毒 (AAV) 是视网膜基因疗法的关键,但面临着挑战. 本综述探讨了克服AAV限制和免疫反应,用于更广泛的视网膜疾病治疗.

关键词:
在 AAV AAV AAV 中.腺相关病毒的病毒.体变种的体变种临床试验是指临床试验中的临床试验.免疫反应的免疫反应.视网膜基因疗法 视网膜基因疗法

更多相关视频

Author Spotlight: Addressing Regulatory Gaps in Molecular Studies by Quantifying Viral Vectors in Complex Matrices07:43

Author Spotlight: Addressing Regulatory Gaps in Molecular Studies by Quantifying Viral Vectors in Complex Matrices

Published on: July 14, 2023

2.1K
Digital Droplet PCR Method for the Quantification of AAV Transduction Efficiency in Murine Retina09:50

Digital Droplet PCR Method for the Quantification of AAV Transduction Efficiency in Murine Retina

Published on: December 25, 2021

4.7K

相关概念视频

Gene Therapy00:59

Gene Therapy

Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be...
25.6K