西

Nayê Balzan Schneider1,2, Erica Caetano Roos3, Ana Lúcia Portella Staub4

  • 1National Institute of Science and Technology for Health Technology Assessment (IATS)- CNPq/Brazil (project: 465518/2014-1), Porto Alegre, Brazil.

概括

在巴西,杜申肌肉缩症 (DMD) 治疗的年度费用为每名患者17,121雷亚尔美元,家庭护理占费用的92%. 这项研究强调了拉丁美洲罕见疾病的重大经济负担.

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