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Updated: Jul 25, 2025

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血友病基因疗法:首先,没有伤害.

Leonard A Valentino1, Radoslaw Kaczmarek2, Glenn F Pierce3

  • 1Rush University, Chicago, Illinois, USA; National Hemophilia Foundation, New York, New York, USA.

Journal of thrombosis and haemostasis : JTH
|June 23, 2023
PubMed
概括

基因疗法为血友病治疗提供了新的希望,但由于历史上的安全问题,需要仔细考虑. 对于考虑用于血友病A和B的腺相关病毒基因治疗的患者来说,知情决策至关重要.

关键词:
有效性 有效性 有效性.基因治疗的基因疗法伤害伤害伤害的伤害血友病 (hemophilia) 是一种血友病.关于安全的安全问题

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