David K Camacho1, Cammille C Go, Brahim Chaqour

  • 1F.M. Kirby Center for Molecular Ophthalmology (DKC, CCG, BC, KSS, AGR), Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania; and Departments of Ophthalmology and Neurology (KSS, AGR), University of Pennsylvania, Philadelphia, Pennsylvania.

概括

基因疗法提供了一种有前途的新方法来治疗视神经病变,通过增强视网膜质细胞的存活率. 这种创新的治疗方法在单次使用后有可能带来长期益处.