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Updated: Jul 22, 2025

Designing, Packaging, and Delivery of High Titer CRISPR Retro and Lentiviruses via Stereotaxic Injection
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开发CRISPR Cas9,衍生技术及其在帕金森病模型构建和潜在治疗方法中的应用

Jiangbo Qu1, Na Liu1, Lu Gao1

  • 1Center for Medical Genetics and Prenatal Diagnosis, Key Laboratory of Birth Defect Prevention and Genetic Medicine of Shandong Health Commission, Key Laboratory of Birth Regulation and Control Technology of National Health Commission of China, Shandong Provincial Maternal and Child Health Care Hospital Affiliated to Qingdao University, Jinan, Shandong, China.

Frontiers in neuroscience
|July 24, 2023
PubMed
概括

CRISPR Cas9基因编辑为帕金森病 (PD) 研究提供了新的途径. 本综述总结了其在创建PD模型和探索未来基因疗法治疗中的应用.

关键词:
克里斯普尔 Cas9 案例帕金森病是帕金森氏症的一种疾病.基因编辑 基因编辑模型动物模型动物精密处理 精密处理

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