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Updated: Jul 21, 2025

Modeling Charcot-Marie-Tooth Disease In Vitro by Transfecting Mouse Primary Motoneurons
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Modeling Charcot-Marie-Tooth Disease In Vitro by Transfecting Mouse Primary Motoneurons

Published on: January 7, 2019

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查尔科-玛丽-牙病治疗的现状

Yuji Okamoto1,2, Hiroshi Takashima1

  • 1Department of Neurology and Geriatrics, Kagoshima University Graduate School of Medical and Dental Sciences, Kagoshima 890-8544, Japan.

Genes
|July 29, 2023
PubMed
概括

由于遗传复杂性,Charcot-Marie-Tooth病 (CMT) 的治疗方法有限. 本综述探讨了常见的CMT类型的有希望的治疗策略和基因疗法,为管理这种遗传性神经病变的未来进展提供了希望.

关键词:
查尔科特玛丽牙病 牙疾病在PXT3003中,我们可以使用PXT3003基因治疗的基因疗法

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