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Isabelle Fajac1, Pierre-Régis Burgel1
1Department of Respiratory Medicine and National Cystic Fibrosis Reference Centre, Cochin Hospital, Assistance Publique Hôpitaux de Paris, 27 rue du faubourg Saint-Jacques, 75014 Paris, France; Université Paris Cité, Inserm U1016, Institut Cochin, 24 rue du faubourg Saint-Jacques, 75014 Paris, France; ERN-LUNG, CF Core Network, Frankfurt, Germany.
囊性纤维化 (CF) 是一种影响多个器官的遗传性疾病. 新的CFTR调节器疗法可以改善肺功能和生存,但对罕见变异的获取和有效性仍然是挑战.
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Published on: April 11, 2018
15:12Purification of the Cystic Fibrosis Transmembrane Conductance Regulator Protein Expressed in Saccharomyces cerevisiae
Published on: May 10, 2014
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